Introduction: Patients with generalized myasthenia gravis (gMG) experience functional impairment due to MG symptoms. This study aimed to assess, from the patient perspective, the symptoms, impacts, and treatment goals of individuals diagnosed with gMG.
This review describes many of the considerations for administration of Luxturna and describes how lessons from experience with Luxturna could lead to additional gene-based treatments of blindness.
The main characteristics of sleep-disordered breathing (SDB) are airflow limitation, chronic intermittent hypoxia, or apnea; which may lead to tissue hypoperfusion and recurrent arousal from sleep.
Peyronie's disease was described by Francois de la Peyronie in 1743, a battlefield surgeon and Commander of the Medical Corps.
We aim to describe the burden of disease in MG including sociodemographic, economical, psychosocial as well as clinical aspects, to compare health-related quality of life (HRQoL) of patients with MG to the general population (genP) and to explore risk factors for a lower HRQoL.
This research aims to identify porphyria-related symptoms between attacks, characterize the frequency, severity, and bothersomeness of these symptoms, and more generally understand the burden of this disease in patients who experience attacks sporadically.
In this review, we provide an overview of the current knowledge on paediatric ADPKD as a future therapeutic target population and its unmet challenges.
Lantheus Holdings, Inc. announced it has entered into multiple strategic agreements with Perspective Therapeutics, Inc. , a radiopharmaceutical company that is pioneering advanced treatment applications for cancers throughout the body
Alnylam Pharmaceuticals, Inc. provided perspective on the positive complete results from the ORION-11 Phase III study of inclisiran, an RNAi...
Asthma affects about 300 million people worldwide, placing an enormous strain on health resources in many countries. Evidence is increasing that asthma is a complex condition with different underlying pathophysiologies.